The Niemann-Pick C1 inhibitor NP3.47 enhances gene silencing potency of lipid nanoparticles containing siRNA

Haitang Wang, Yuen Yi C. Tam, Sam Chen, Josh Zaifman, Roy van der Meel, Marco A. Ciufolini, Pieter R. Cullis

Research output: Contribution to journalArticleAcademicpeer-review

34 Citations (SciVal)

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Biochemistry, Genetics and Molecular Biology